REGENXBIO Inc. (RGNX) announced positive data from the Phase I/II/III CAMPSIITE trial of clemidsogene lanparvovec or RGX-121 for the treatment of patients with Mucopolysaccharidosis Type II, also known as Hunter syndrome. Primary endpoint of CSF HS D2S6 reduction at week 16 was met.
The company submitted these longer-term pivotal results to the FDA in response to an information request in the ongoing Biologics License Application review of RGX-121. The FDA is expected to make a decision on the application by February 8, 2026.
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May 01, 2026 15:54 ET Central banks dominated the economics news flow this week with almost all major ones announcing their latest policy decisions and many boosted expectations for a rate hike in June. In other news, several countries released the preliminary data for first quarter economic growth. In the U.S., comments by Fed Chair Jerome Powell were also in focus as his term ends this month.