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Can Wave Life Sciences Make Waves With Forward-53 DMD Trial Data?

By RTTNews Staff Writer   ✉  | Published:  | Google News Follow Us  | Join Us
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Duchenne muscular dystrophy, or DMD in short, is a rare and progressive genetic muscle disease caused by mutations in the dystrophin-encoding DMD gene and it occurs primarily in boys. DMD patients lack dystrophin, a critical membrane-stabilizing protein, which leads to muscle degeneration and weakness. The DMD gene contains 79 exons which are pieces of coding DNA that encode the protein dystrophin. Exon-skipping is one of the therapies that can restore the expression of partially functional dystrophin protein. Approximately 8%-10% of DMD patients have mutations amenable to treatment with an exon 53 skipping therapy.

The stock we are bringing to your attention today is that of Wave Life Sciences Ltd. (WVE), which is developing a treatment for boys with Duchenne muscular dystrophy (DMD) amenable to exon 53 skipping.

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Global Economics Weekly Update: May 11 – May 15, 2026

May 15, 2026 15:25 ET
Apart from the confirmation of Kevin Warsh as the next Fed chair, the main news on the economics front this week included key price data from the U.S. and the first quarter economic growth figures from major economies. Both consumer prices and producer costs have started to reflect the effect of supply shocks due to the Middle East conflict. In Europe, GDP data was in focus, while inflation data from China dominated the news flow in Asia.

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